What Is Gene Therapy?

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Classic Gene Therapy is pretty straight forward, it's been around, I mean we've understood it for a long time, and that is the idea that you identify a gene that's defective. Presumably, it produces either a defective protein or it doesn't secrete a protein at all, and patients develop very severe diseases.

So, right now it is big [xx] with fleeing often times, leads to blindness, especially the more severe cases in the teenage years 20 to 30s. The idea that you could identify that gene and replace that gene, that's been a very, it's kind of been a holy grail.