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How can a bone marrow transplant treat an inherited metabolic disorder?

In some cases, a bone marrow transplant can help treat an inherited metabolic disorder, such as mucopolysaccharidoses. In the case of mucopolysaccharidoses, the body cannot break down and store the sugar molecules it needs to build healthy tissue, and the deposits instead accumulate in other areas of the body. If caught early, a bone marrow transplant can sometimes help to slow the progress of the disorder or stop it altogether. But this treatment is still in development; further, it is not always effective and may even result in disbility or death.

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Important: This content reflects information from various individuals and organizations and may offer alternative or opposing points of view. It should not be used for medical advice, diagnosis or treatment. As always, you should consult with your healthcare provider about your specific health needs.