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What are the treatments for Niemann-Pick (NP) disease?

There is currently no effective treatment for Type A Niemann-Pick (NP) disease. Bone marrow transplantation has been attempted in a few patients with Type B NP disease, and encouraging results have been reported. The development of enzyme replacement and gene therapies might also be helpful for those with Type B. Individuals with Types C and D NP disease are frequently placed on a low-cholesterol diet, but its clinical benefit is not convincing.

This answer is based on source information from the National Institute of Neurological Disorders and Stroke.

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