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What are the treatment options for Fabry disease?

There is no cure available for Fabry disease.  However, enzyme replacement therapy is available to replace the missing enzyme that causes Fabry issues.  In addition to enzyme replacement therapy, other medications are used to treat disease symptoms.  Protein in the urine can be treated with categories of medications called ACE inhibitors and ARBs.  Pain and  burning sensations in the arms and legs can be treated with anticonvulsants. Gastrointestinal problems can be treated with metroclopramide.  Low dose aspirin is given to decrease stroke risk.  Those who develop more serious symptoms like heart and kidney disease may need surgery, transplants, or dialysis.

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